Duchenne Muscular Dystrophy Global Clinical Trials Review, H2, 2017

Published : Jul-2017

No. of Pages : 166

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Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 5
Report Guidance 6
GlobalData Clinical Trials Report Coverage 7
Clinical Trials by Region 8
Clinical Trials and Average Enrollment by Country 9
Top Five Countries Contributing to Clinical Trials in Asia-Pacific 12
Top Five Countries Contributing to Clinical Trials in Europe 13
Top Countries Contributing to Clinical Trials in North America 14
Top Countries Contributing to Clinical Trials in Middle East and Africa 15
Top Countries Contributing to Clinical Trials in Central and South America 16
Clinical Trials by G7 Countries: Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials 17
Clinical Trials by Phase in G7 Countries 19
Clinical Trials in G7 Countries by Trial Status 20
Clinical Trials by E7 Countries: Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials 22
Clinical Trials by Phase in E7 Countries 24
Clinical Trials in E7 Countries by Trial Status 25
Clinical Trials by Phase 26
In Progress Trials by Phase 27
Clinical Trials by Trial Status 28
Clinical Trials by End Point Status 30
Subjects Recruited Over a Period of Time 31
Clinical Trials by Sponsor Type 32
Prominent Sponsors 33
Top Companies Participating in Duchenne Muscular Dystrophy Therapeutics Clinical Trials 35
Prominent Drugs 37
Latest Clinical Trials News on Duchenne Muscular Dystrophy 38
Jul 18, 2017: PTC Therapeutics Announces Publication of Data from ACT DMD in The Lancet 38
Jun 26, 2017: Antisense Therapeutics to Enter Clinical Development in Duchenne Muscular Dystrophy 38
Jun 23, 2017: Catabasis Pharmaceuticals to Present Results from the MoveDMD Trial of Edasalonexent at the 2017 PPMD Annual Connect Conference 39
Jun 22, 2017: Summit Presents Data From Phase 1 Clinical Programme of Ezutromid at the European Paediatric Neurology Society Congress 39
Jun 22, 2017: New Analyses of Translarna (ataluren) Data from ACT DMD Presented at the 12th Annual European Pediatric Neurology Society Congress 39
Jun 14, 2017: CureDuchenne to Host Webinar with Santhera Pharmaceuticals on SIDEROS Trial 40
May 30, 2017: Pfizer Completes Enrollment of Phase 2 Study of Domagrozumab (PF- 06252616) in Duchenne Muscular Dystrophy 40
May 23, 2017: New Analysis of ACT DMD Placebo Data on Corticosteroids Presented at International Society for Pharmacoeconomics and Outcomes Research 22nd Annual International Meeting 40
May 16, 2017: Santhera to Present Data and Host Symposium on Pulmonary Function in Duchenne Muscular Dystrophy at the American Thoracic Society 113th Annual Conference 40
May 15, 2017: Summit Completes Enrolment of PhaseOut DMD, a Phase 2 Clinical Trial of Ezutromid in Patients with DMD 41
May 11, 2017: New Preclinical Data Support SGT-001 As A Novel Treatment Approach For Duchenne Muscular Dystrophy 42
May 03, 2017: GTx Announces Results from Preclinical Studies of SARMs in Duchenne Muscular Dystrophy Models Published in Human Molecular Genetics 42
Clinical Trial Profile Snapshots 43
Appendix 164
Abbreviations 164
Definitions 164
Research Methodology 165
Secondary Research 165
About GlobalData 166
Contact Us 166
Source 166

List of Tables
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Region, 2017* 8
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials and Average Enrollment by Top Countries, 2017* 10
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials In Progress by Top Countries, 2017* 11
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Asia-Pacific, Top Five Countries, 2017* 12
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Europe, Top Five Countries, 2017* 13
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, North America, Top Countries, 2017* 14
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Middle East and Africa, Top Countries, 2017* 15
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Central and South America, Top Countries, 2017* 16
Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials, G7 Countries (%), 2017* 18
Duchenne Muscular Dystrophy Therapeutics, G7 Countries, Clinical Trials by Phase, 2017* 19
Duchenne Muscular Dystrophy Therapeutics, G7 Countries, Clinical Trials by Trial Status, 2017* 21
Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials, E7 Countries (%), 2017* 23
Duchenne Muscular Dystrophy Therapeutics, E7 Countries, Clinical Trials by Phase, 2017* 24
Duchenne Muscular Dystrophy Therapeutics, E7 Countries, Clinical Trials by Trial Status, 2017* 25
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Phase, 2017* 26
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials In Progress by Phase 2017* 27
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Trial Status, 2017* 29
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, by End Point Status, 2017* 30
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2012-2016 31
Duchenne Muscular Dystrophy Therapeutics Market, Global, Clinical Trials by Sponsor Type, 2017* 32
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Key Sponsors, 2017* 34
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Top Companies by Phase, 2017* 36
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Ongoing Clinical Trials by Prominent Drugs, 2017* 37

List of Figures
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Region (%), 2017* 8
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials and Average Enrollment by Top Countries, 2017* 9
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials In Progress by Top Countries, 2017* 11
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Asia-Pacific, Top Five Countries (%), 2017* 12
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Europe, Top Five Countries (%), 2017* 13
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, North America, Top Countries (%), 2017* 14
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Middle East and Africa, Top Countries (%), 2017* 15
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Central and South America, Top Countries (%), 2017* 16
Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials, G7 Countries (%), 2017* 17
Duchenne Muscular Dystrophy Therapeutics, G7 Countries, Clinical Trials by Phase, 2017* 19
Duchenne Muscular Dystrophy Therapeutics, G7 Countries, Clinical Trials by Trial Status, 2017* 20
Proportion of Duchenne Muscular Dystrophy to Genetic Disorders Clinical Trials, E7 Countries (%), 2017* 22
Duchenne Muscular Dystrophy Therapeutics, E7 Countries, Clinical Trials by Phase, 2017* 24
Duchenne Muscular Dystrophy Therapeutics, E7 Countries, Clinical Trials by Trial Status, 2017* 25
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Phase (%), 2017* 26
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials In Progress by Phase, 2017* 27
Duchenne Muscular Dystrophy Therapeutics, Global, Clinical Trials by Trial Status, 2017* 28
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, by End Point Status, 2017* 30
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2012-2016 31
Duchenne Muscular Dystrophy Therapeutics Market, Global, Clinical Trials by Sponsor Type (%), 2017* 32
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Key Sponsors, 2017* 33
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Top Companies by Phase, 2017* 35
Duchenne Muscular Dystrophy Therapeutics Clinical Trials, Global, Ongoing Clinical Trials by Prominent Drugs, 2017* 37
GlobalData Methodology 165

Filed in: Pharmaceutical

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